biomarkers
cerebral spinal fluid
clinical trials
Frank Bennett
gene silencing
huntingtin
Huntington's disease
Ionis Pharmaceuticals
IONIS-HTT-Rx
neurofilament
open-label extension
safety
tolerability
Ionis Huntington’S Illness Drug A Footstep Closer To A Critical Stage Two Study
Ionis Pharmaceuticals has made 2 positive announcements almost the historic Phase 1 clinical case of its gene-silencing drug for Huntington’s disease…